Gene Therapy News
World AIDS Day: How the World Is Still Fighting the Disease 35 Years After Its Discovery
It's been 35 years since researchers from the U.S. Centers for Disease Control and Prevention first reported on a mysterious illness that was infecting and killing healthy young men. The CDC report from 1981 was the first time AIDS was ever mentioned in medical literature. In those early days,
No designer babies, but gene editing to avoid disease? Maybe
Altering human heredity sounds sci-fi, but a major new ethics report is leaving open the possibility that one day scientists might try that to fight some serious genetic diseases
Family Isolated for 2 Years Hoping to Qualify for Daughter's Experimental Treatment
For nearly two years, more than 700 days, the O'Neill family stayed in isolation in their South Carolina home in an effort to save their daughter Eliza. Eliza, now 6, was diagnosed with a rare degenerative disease called Sanfilippo Syndrome Type A two years ago. The disease, sometime's called
Child With Rare Disease That Reverses Development Hasn't Lost Her Smile
When Olivia Thurston was born on January 15, 2008, weighing in at 8 pounds and 6 ounces, she was a happy and healthy baby and continued to develop normally in her first years. But at the age of 3, her progress changed. Her speech was limited and she became increasingly clumsy; she suffered from
Joe Biden's Full Interview With Robin Roberts on Cancer Moonshoot Task Force
The vice president talks exclusively to "Good Morning America" co-anchor Robin Roberts about his the Cancer Moonshot task force and the presidential race.
Hollywood Producer Fights to Save Daughters From Rare Disease
Gordon Gray's daughters Charlotte and Gwenyth were diagnosed with Batten CLN6, a degenerative brain disorder.
Family on a Mission to Find a Cure for Daughter's Rare Genetic Disease
Olivia Burtwistle and her family see a glimmer of hope for a cure in Sioux Falls, South Dakota, home to one of the country's leading medical systems, Sanford Health.
Adult Stem Cell Therapy Offers Hope for Those With Rare Genetic Diseases
Olivia Burtwistle grew as a typically curious and energetic child until soon after her fourth birthday, when her parents began to notice changes, including a “rapid decline” in Olivia’s vision. The Burtwistles, Brad and Julie, met with doctors around the country searching for answers for Olivia. At
Why Ex-Facebook President Sean Parker Is Betting $250M on This Cancer Treatment
The battle to cure cancer just got a serious boost thanks to former Facebook President Sean Parker , who has pledged to donate $250 million to research a breakthrough area of cancer treatment called immunothearpy. Immunotherapy treatments, which work by harnessing the body's immune system to battle