Gene Therapy News
Family Isolated for 2 Years Hoping to Qualify for Daughter's Experimental Treatment
For nearly two years, more than 700 days, the O'Neill family stayed in isolation in their South Carolina home in an effort to save their daughter Eliza. Eliza, now 6, was diagnosed with a rare degenerative disease called Sanfilippo Syndrome Type A two years ago. The disease, sometime's called
Child With Rare Disease That Reverses Development Hasn't Lost Her Smile
When Olivia Thurston was born on January 15, 2008, weighing in at 8 pounds and 6 ounces, she was a happy and healthy baby and continued to develop normally in her first years. But at the age of 3, her progress changed. Her speech was limited and she became increasingly clumsy; she suffered from
Joe Biden's Full Interview With Robin Roberts on Cancer Moonshoot Task Force
The vice president talks exclusively to "Good Morning America" co-anchor Robin Roberts about his the Cancer Moonshot task force and the presidential race.
Hollywood Producer Fights to Save Daughters From Rare Disease
Gordon Gray's daughters Charlotte and Gwenyth were diagnosed with Batten CLN6, a degenerative brain disorder.
Family on a Mission to Find a Cure for Daughter's Rare Genetic Disease
Olivia Burtwistle and her family see a glimmer of hope for a cure in Sioux Falls, South Dakota, home to one of the country's leading medical systems, Sanford Health.
Adult Stem Cell Therapy Offers Hope for Those With Rare Genetic Diseases
Olivia Burtwistle grew as a typically curious and energetic child until soon after her fourth birthday, when her parents began to notice changes, including a “rapid decline” in Olivia’s vision. The Burtwistles, Brad and Julie, met with doctors around the country searching for answers for Olivia. At
Why Ex-Facebook President Sean Parker Is Betting $250M on This Cancer Treatment
The battle to cure cancer just got a serious boost thanks to former Facebook President Sean Parker , who has pledged to donate $250 million to research a breakthrough area of cancer treatment called immunothearpy. Immunotherapy treatments, which work by harnessing the body's immune system to battle
Infant Goes Into Remission Thanks to Cancer Treatment Breakthrough With 'Edited' Cells
A breakthrough technology has given hope to a family who thought their baby daughter may not survive to her second birthday. Layla Richards was diagnosed with leukemia last year at 14 weeks old, according to the Great Ormond Street Hospital in London. While her doctors tried multiple treatments,
Bland Family Speaks Out; USAG Loretta Lynch: Federal Charges for Dylann Roof; FAA Considering Ways to Strengthen Planes Against Bird Collisions
Family of Sandra Bland speaks out; U.S. Attorney General Loretta Lynch announces federal charges for Dylann Roof; FAA considering ways to make planes stronger against bird collisions.
Mutation Discovered in Cannibal Tribe Might Stop Deadly Brain Disease
The DNA of tribes in a remote area of Papa New Guinea may someday help scientists find a way to protect people from certain degenerative brain diseases, including the illness commonly called "mad cow" disease. While studying the Fore population in Papa New Guinea, which has practiced cannibalism in